FDA Approves First Treatment for Niemann-Pick Disease, Type C - FDA.gov

1. FDA Approves First Treatment for Niemann-Pick Disease, Type C  FDA.gov
2. FDA approves first drug for rare neuron disease, Niemann-Pick type C  STAT
3. US FDA approves Zevra's treatment for rare genetic disease  Yahoo Finance
4. After prior snub, Zevra clinches FDA approval for rare lysosomal storage disorder drug Miplyffa  FiercePharma
5. FDA Approves Zevra's Miplyffa for Niemann-Pick Disease Type C -- 2nd Update  MarketWatch